Scientific article
OA Policy
English

Therapeutic siRNA silencing in inflammatory monocytes in mice

Published inNature biotechnology, vol. 29, no. 11, p. 1005-1010
Publication date2011-10-09
First online date2011-10-09
Abstract

Excessive and prolonged activity of inflammatory monocytes is a hallmark of many diseases with an inflammatory component. In such conditions, precise targeting of these cells could be therapeutically beneficial while sparing many essential functions of the innate immune system, thus limiting unwanted effects. Inflammatory monocytes-but not the noninflammatory subset-depend on the chemokine receptor CCR2 for localization to injured tissue. Here we present an optimized lipid nanoparticle and a CCR2-silencing short interfering RNA that, when administered systemically in mice, show rapid blood clearance, accumulate in spleen and bone marrow, and localize to monocytes. Efficient degradation of CCR2 mRNA in monocytes prevents their accumulation in sites of inflammation. Specifically, the treatment attenuates their number in atherosclerotic plaques, reduces infarct size after coronary artery occlusion, prolongs normoglycemia in diabetic mice after pancreatic islet transplantation, and results in reduced tumor volumes and lower numbers of tumor-associated macrophages.

Keywords
  • Animals
  • Atherosclerosis / therapy
  • Blood Glucose
  • Diabetes Mellitus / surgery
  • Diabetes Mellitus / therapy
  • Disease Models, Animal
  • Gene Silencing
  • Graft Survival / genetics
  • Humans
  • Inflammation / therapy
  • Islets of Langerhans Transplantation
  • Macrophages / drug effects
  • Mice
  • Mice, Inbred C57BL
  • Monocytes / metabolism
  • Myocardial Infarction / prevention & control
  • Myocardial Infarction / therapy
  • Nanoparticles / chemistry
  • RNA, Small Interfering / therapeutic use
  • Receptors, CCR2 / antagonists & inhibitors
  • Receptors, CCR2 / genetics
Affiliation entities Not a UNIGE publication
Funding
  • NHLBI NIH HHS [HHSN268201000044C]
  • NCI NIH HHS [P50 CA086355]
  • NIAID NIH HHS [R01 AI084880]
  • NIBIB NIH HHS [R01-EB006432]
  • PHS HHS [268201000044C]
Citation (ISO format)
LEUSCHNER, Florian et al. Therapeutic siRNA silencing in inflammatory monocytes in mice. In: Nature biotechnology, 2011, vol. 29, n° 11, p. 1005–1010. doi: 10.1038/nbt.1989
Main files (2)
Article (Published version)
accessLevelRestricted
Article (Accepted version)
Identifiers
Additional URL for this publicationhttps://www.nature.com/articles/nbt.1989
Journal ISSN1087-0156
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20downloads

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