• Home
  1. Home
  2. Impact of imiglucerase supply constraint on the therapeutic management and course of disease in French patients with Gaucher disease type 1
Scientific article
OA Policy
English

Impact of imiglucerase supply constraint on the therapeutic management and course of disease in French patients with Gaucher disease type 1

ContributorsStirnemann, Jérôme; Rose, Christian; De Roux Serratrice, Christineorcid; Dalbies, Florence; Lidove, Olivier; Masseau, Agathe; Pers, Yves-Marie; Baron, Camille; Belmatoug, Nadia
Published inOrphanet journal of rare diseases, vol. 10, 62
Publication date2015
Abstract

In 2009, a worldwide supply constraint of imiglucerase led to treatment modifications or interruptions for patients with Gaucher disease (GD) type 1. In France, joint treatment recommendations were issued to protect the most vulnerable patients. This observational study evaluated the impact of imiglucerase treatment modifications on the clinical and biological course of GD.

Affiliation entities
Research groups
Citation (ISO format)
STIRNEMANN, Jérôme et al. Impact of imiglucerase supply constraint on the therapeutic management and course of disease in French patients with Gaucher disease type 1. In: Orphanet journal of rare diseases, 2015, vol. 10, p. 62. doi: 10.1186/s13023-015-0275-0
Main files (1)
Article (Published version)
accessLevelPublic
Identifiers
Journal ISSN1750-1172
580views
378downloads

Technical informations

Creation07/11/2015 13:41:00
First validation07/11/2015 13:41:00
Update14/03/2023 23:58:50
Status update14/03/2023 23:58:49
Last indexation31/10/2024 02:18:21
All rights reserved by Archive ouverte UNIGE and the University of GenevaunigeBlack