en
Scientific article
Editorial
English

Tamoxifen in Duchenne muscular dystrophy – promising first results

ContributorsRuegg, Urs
Published inNeuromuscular disorders, vol. 31, no. 9, p. 801-802
Publication date2021-09-09
Abstract

The most common diseases are of polygenic origin. Since early last century, these are being treated with drugs that act downstream of the genetic hurdle. This strategy has saved millions of lives. The advent of genetics revealed the molecular basis of diseases of monogenic origin, including the neuromuscular ones. It was tempting to believe that the defective genes can be repaired with novel chemicals, with a cure being “just down the road”.

eng
Keywords
  • Duchenne muscular dystrophy
  • Pharmacology.
  • Clinical Trial
  • Tamoxifen
  • Patients
Citation (ISO format)
RUEGG, Urs. Tamoxifen in Duchenne muscular dystrophy – promising first results. In: Neuromuscular disorders, 2021, vol. 31, n° 9, p. 801–802. doi: 10.1016/j.nmd.2021.09.003
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Article (Published version)
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Identifiers
ISSN of the journal0960-8966
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