Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy
Published inBiology of blood and marrow transplantation, vol. 26, no. 10, p. 1819-1827
Publication date2020-10
First online date2020-07-09
Abstract
Keywords
- Adenosine Deaminase / genetics
- Agammaglobulinemia
- Busulfan
- Child
- Genetic Therapy
- Hematopoietic Stem Cell Transplantation
- Humans
- Infant
- Severe Combined Immunodeficiency / genetics
- Severe Combined Immunodeficiency / therapy
- Transplantation Conditioning
- Adenosine deaminase
- SCID
- Busulfan
- Pharmacokinetics
- Gene therapy
- Clinical trials
Research group
Citation (ISO format)
BRADFORD, Kathryn L et al. Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy. In: Biology of blood and marrow transplantation, 2020, vol. 26, n° 10, p. 1819–1827. doi: 10.1016/j.bbmt.2020.07.004
Secondary files (1)
Identifiers
- PID : unige:156649
- DOI : 10.1016/j.bbmt.2020.07.004
- PMID : 32653625
- PMCID : PMC7529956
ISSN of the journal1083-8791